For some gene therapies, achieving 100% cell delivery is unnecessary—delivering 1% of an enzyme to just one tissue type can be sufficient if the enzyme is secreted into the bloodstream, allowing for example a muscle to be temporarily converted to part of the immune system for vaccine delivery.
factualpending
Speaker
George ChurchEvidence Quote
“For example, for some therapies you just need to get 1% because that 1% can produce some missing enzyme. And that 1% doesn't have to necessarily be in its normal place.”
Created: 8/11/2026, 6:40:03 AM
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